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podcast

AI in LSD Diagnosis

1 minute

Dr. Karolina Stepien

Adult Metabolic Consultant

Prof. Jecko Thachil

Consultant Haematologist

download

Fabry Disease Referral Piece Tile

video

Fabry Outcome Survey Thumbnail

Two Decades of Experience from the Fabry Outcome Survey demonstrating the long-term effectiveness of agalsidase alfa enzyme replacement therapy.

Dr. Uma Ramaswami, FRCPCH, MD